Contents
CHAPTER 1: Disease-modifying Therapies in Spinal Muscular Atrophy and Duchenne Muscular Dystrophy: A Rapidly Changing Scenario
CHAPTER 2: Refractory Myasthenia: Management Strategies
CHAPTER 3: Congenital Myasthenic Syndromes: Genetic Spectrum and Management
CHAPTER 4: Idiopathic Inflammatory Myopathies and Current Immunology
CHAPTER 5: Updates on Limb-girdle Dystrophies and Gene Therapies
CHAPTER 6: Clinical Utility and Interpretation of Genetic Testing in Neuromuscular Disorders
CHAPTER 7: Facioscapulohumeral Dystrophy: Update on Treatment
CHAPTER 8: Riboflavinopathies: Potentially Treatable Disorders
CHAPTER 9: Mitochondrial Disorders: A Neuromuscular Perspective
CHAPTER 10: Therapeutic Advances in Nodoparanodopathies
CHAPTER 11: Chronic Inflammatory Demyelinating Polyradiculoneuropathy and its "Variants": Current Treatment Recommendations
CHAPTER 12: Neuromuscular Imaging: MRI and Ultrasound
CHAPTER 13: Hirayama Disease/Monomelic Amyotrophy: Recent Advances and Surgical Management
CHAPTER 14: Recent Classification and Emerging Therapies in Charcot-Marie-Tooth Disease
CHAPTER 15: Genetics of Amyotrophic Lateral Sclerosis and Implications for Therapy